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    The 2025 Rett Gazette

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Neurogene Announces First Participant Dosed in Embolden™ Registrational Trial of NGN-401 Gene Therapy for Rett Syndrome

Neurogene Announces Positive Regulatory Update for NGN-401 Gene Therapy in Rett Syndrome with Plans to Initiate Dosing in Embolden™ Registrational Trial in Q4 2025

Neurogene Reports Second Quarter 2025 Financial Results and Highlights Recent Updates

Neurogene Announces Registrational Trial Design for Embolden™ Study of NGN-401 Gene Therapy for Rett Syndrome (Community Letter)

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Neurogene Announces Registrational Trial Design for Embolden™ Study of NGN-401 Gene Therapy for Rett Syndrome

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Neurogene Updates on Program & Risk Mitigation Strategies (Community Letter)

Neurogene Reports Fourth Quarter and Full Year 2024 Financial Results and Highlights Recent Updates

Update on Patient SAE & Discontinuation of High Dose Protocol (Community Letter)

Update on Patient SAE (Community Letter)

Neurogene Provides Update on NGN-401 Gene Therapy Clinical Trial for Rett Syndrome

Neurogene Community Letter

Neurogene Reports Positive Interim Efficacy Data from First Four Low-Dose Pediatric Participants in NGN-401 Gene Therapy Clinical Trial for Rett Syndrome

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