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Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

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Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

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Jane Doe - Charleston, SC

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Acadia Pharmaceuticals Acquires International Rights to Trofinetide

Thursday, July 13, 2023

BIG NEWS for our international Rett syndrome community! Today, Acadia Pharmaceuticals announced they have acquired the rights to make trofinetide available for the treatment of Rett syndrome across the globe. READ THE PRESS RELEASE This is an essential starting point in ensuring ALL Rett families have access to this treatment. Acadia already retains the rights … Read More

RettAway Reflections

Tuesday, July 11, 2023

By Samantha Brant, Family & Community Engagement Manager, and mom to Macy As I returned home from this year’s RettAway at Morgan’s Inspiration Island, my heart swelled with not only pride but warmth. I attended the last RettAway in 2017 as simply a parent to a 3-year-old little peanut, Macy. And I took so much … Read More

IRSF Welcomes Three New Members to its Board of Directors

Monday, July 10, 2023

The International Rett Syndrome Foundation (IRSF), a mission-driven advocacy foundation focused on funding research and supporting families impacted by Rett syndrome, today announced the expansion of its Board of Directors. Mary Engel, Laura Stoppel, and Steve Wood have been appointed to the IRSF Board, effective July 1, 2023. “We are delighted to welcome these new … Read More

Clinical Trial Updates from Taysha & Anavex

Wednesday, June 28, 2023

We are excited to share news from two pharmaceutical companies working on potential treatments and cures for Rett syndrome. Taysha Gene Therapies Taysha Gene Therapies shared that they are encouraged by the initial clinical observations of the first adult patient dosed in their TSHA-102 REVEAL Phase 1/2 gene therapy trial in Canada. Further clinical updates … Read More

Neurogene Announces Locations & Opens Enrollment for US Gene Therapy Clinical Trial

Monday, June 12, 2023

We’re excited to share that today Neurogene announced the locations and began enrolling for the first U.S. Phase 1/2 clinical trial of their investigational gene therapy, NGN-401. Enrollment at Texas Children’s Hospital begins today, with enrollment at Children’s Hospital Colorado and Boston Children’s Hospital anticipated to open soon. The trial will enroll five (5) females aged … Read More

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Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, duo ne vero molestie invidunt.

Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

Ut nec modus option, ex est maiestatis contentiones disputationi. Pri in vidit definiebas, ex eum vivendo consulatu, cu mundi nostrud pertinax eam. Nec timeam fabellas no, idque audire nec ea. Mel an modo magna minimum, at posse invidunt mea. Ius no doctus patrioque, dicam legere dissentias qui ea. Mel ei solum ullum fastidii, sit eius brute doctus eu.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Personnel Module

John Doe

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, du

Jane Doe

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex.

Ridens Pertinax

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, du

Tom Smith

Lorem ipsum dolor sit amet, consectetur adipiscing elit. Phasellus eu massa nisl. Maecenas eget enim vitae lectus bibendum malesuada a id urna. Pellentesque convallis felis et nibh gravida, vitae bibendum lacus blandit. Fusce pharetra ac nisl ac sagi

Column 1

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Lorem ipsum dolor sit amet, consectetur adipiscing elit. Phasellus eu massa nisl. Maecenas eget enim vitae lectus bibendum malesuada a id urna. Pellentesque