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Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

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Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

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Jane Doe - Charleston, SC

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Advocating for YOU: Rare Disease Week on Capitol Hill

Wednesday, March 20, 2024

IRSF works tirelessly to advocate for you and your loved one with Rett syndrome. Our work takes many forms, our persistence is often unseen, and our successes are the result of countless hours spent meeting with, raising awareness, and educating key decision-makers on the needs of our Rett community. Last month, our advocacy efforts were … Read More

Neurogene Announces Expansion of Gene Therapy Clinical Trial

Monday, March 4, 2024

Today, Neurogene announced plans to expand and more rapidly enroll patients their Phase 1/2 clinical trial of investigational gene therapy NGN-401. For the full press release, click here. Key Facts: The study will now expand to include a total of 16 pediatric participants (age 4-10). Cohort 1 (low dose group) will increase from 5 to … Read More

Taysha Gene Therapies Adolescent & Adult Study Expanded to U.S.

Thursday, February 29, 2024

Today, Taysha Gene Therapies shared several exciting updates on their REVEAL Phase 1/2 clinical trial of investigational gene therapy TSHA-102: The study will now expand to include adolescent and adult patients in the U.S. (age 12+ protocol). The dosing of the first cohort (low dose) is complete in the adult study in Canada with clinical … Read More

My Rett Ally: Revolutionizing Care Management for Rett Families

Thursday, January 11, 2024

On a recent visit to the emergency room, it took just seconds for Samantha Brant to pull up a detailed, up-to-date medication list for her daughter, Macy. Macy lives with Rett syndrome and Samantha, like all families with a loved one with Rett, must keep meticulous records of health documents to ensure the best possible … Read More

Taysha Gene Therapies Doses First Pediatric Patient in U.S. Gene Therapy Clinical Trial

Wednesday, January 10, 2024

Taysha Gene Therapies today announced the dosing of the first pediatric patient in their REVEAL Phase 1/2 trial of investigational gene therapy TSHA-102. For Taysha’s full press release, click here. Key Facts: The first female pediatric patient was dosed at RUSH University Medical Center in Chicago, an IRSF-designated Center of Excellence. The REVEAL Phase 1/2 … Read More

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Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, duo ne vero molestie invidunt.

Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

Ut nec modus option, ex est maiestatis contentiones disputationi. Pri in vidit definiebas, ex eum vivendo consulatu, cu mundi nostrud pertinax eam. Nec timeam fabellas no, idque audire nec ea. Mel an modo magna minimum, at posse invidunt mea. Ius no doctus patrioque, dicam legere dissentias qui ea. Mel ei solum ullum fastidii, sit eius brute doctus eu.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Personnel Module

John Doe

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, du

Jane Doe

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex.

Ridens Pertinax

Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, du

Tom Smith

Lorem ipsum dolor sit amet, consectetur adipiscing elit. Phasellus eu massa nisl. Maecenas eget enim vitae lectus bibendum malesuada a id urna. Pellentesque convallis felis et nibh gravida, vitae bibendum lacus blandit. Fusce pharetra ac nisl ac sagi

Column 1

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Lorem ipsum dolor sit amet, consectetur adipiscing elit. Phasellus eu massa nisl. Maecenas eget enim vitae lectus bibendum malesuada a id urna. Pellentesque