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Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, duo ne vero molestie invidunt.

Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

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Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

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Neurogene Announces First Rett Syndrome Gene Therapy Trial in U.S.

Monday, January 23, 2023

We’re excited to share that Neurogene announced today that the FDA approved their Investigational New Drug Application (IND) to launch a clinical trial for their gene therapy treatment NGN-401 in 2023 in pediatric females. This is the second gene therapy clinical study in Rett syndrome currently underway and the very first gene therapy clinical trial … Read More

IRSF Receives $500,000 Donation from Vezbi Super App

Tuesday, January 3, 2023

International Rett Syndrome Foundation (IRSF) is proud to announce that it is the recipient of a $500,000 donation from the Vezbi Super App as part of its Project Seva. Along with the donation, Vezbi will be creating custom Micro-apps and Communities for use by IRSF and the community of families impacted by Rett syndrome that … Read More

Flu, COVID, & RSV: A Message to our Rett Community

Thursday, December 8, 2022

By Dr. Tim Benke, IRSF Medical Advisor As many of you know, the United States is currently facing the triple impact of flu, RSV, and COVID-19. These respiratory illnesses are currently circulating at levels higher than usual for this time of year, creating a surge of patients seeking care in clinical offices, emergency rooms, and … Read More

Taysha Begins Recruitment for Gene Therapy Trial

Thursday, November 17, 2022

Next Huge Milestone for Rett The last 12 months have been an unprecedented time for Rett syndrome. In December 2021, Acadia Pharmaceuticals reported that the first (and only) Phase 3 clinical trial in Rett syndrome had positive results. As hopefully many of you know, Acadia submitted a New Drug Application to the FDA for approval … Read More

Your Voice Matters to the FDA & Pharmaceutical Industry

Thursday, October 13, 2022

By Dr. Dominique Pichard, IRSF CSO – The patient voice has increasingly become a focus for the Food and Drug Administration (FDA) in the drug development process. Thanks to years of advocacy from patients and caregivers, the FDA has developed mechanisms to hear the patient voice and has encouraged pharmaceutical companies to increasingly include the … Read More

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Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, duo ne vero molestie invidunt.

Mei qualisque adolescens reprimique ea, sit tempor invenire at. Id atqui aliquip mel, ei tibique minimum eum, ex pri aliquip persecuti appellantur. Nulla conclusionemque eos ei, et usu animal integre volumus, quidam suscipit molestiae eos ea. Nec soleat concludaturque ea, quodsi dolores suavitate sed at, ea alia sonet elitr duo. Fabellas adolescens pro ea. Quot lorem dicam pri ex, qui an tritani perfecto.

Ut copiosae signiferumque sed, pri ad alii debitis prodesset, vis ea elit augue volumus. Nonumy impedit reprehendunt vel cu, illud audiam nec ne. Et nec nisl libris, nec ex aperiri oportere temporibus, quo nihil numquam ut. Eu habemus deleniti singulis duo. Mei melius intellegam ad.

Ut nec modus option, ex est maiestatis contentiones disputationi. Pri in vidit definiebas, ex eum vivendo consulatu, cu mundi nostrud pertinax eam. Nec timeam fabellas no, idque audire nec ea. Mel an modo magna minimum, at posse invidunt mea. Ius no doctus patrioque, dicam legere dissentias qui ea. Mel ei solum ullum fastidii, sit eius brute doctus eu.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

Mea clita ceteros reprehendunt ad, et mei docendi recteque, nec saepe malorum quaerendum ei. Ut wisi ceteros has, porro noster facilisis ex nam, hinc tantas ea eos. Persius eruditi ut mea, graecis salutatus conclusionemque id pro. Eu nec graeci aliquip. Eos ex esse lorem alterum, et utinam putent mei, ei imperdiet cotidieque vim. Fierent honestatis eu his, cu consequat assueverit has, justo nihil referrentur cu eam.

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Jane Doe

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Riley Smith

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Lorem ipsum dolor sit amet, et unum docendi nam, ea mei iriure insolens, nec te prima invenire. At brute lorem adolescens usu, vis ne clita alterum. Dicta animal facilisi duo cu. Ridens pertinax conceptam eam ex. Eum no dicant melius definitionem, du

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