IRSF APPROACH

Our Scientific Strategy

IRSF’s highly comprehensive scientific program in Rett syndrome—bolstered by unprecedented industry partnerships—includes the advancement of genetic approaches and developing drugs that improve quality of life, as well as the development of a clinical research network that brings treatments to families.

Over the last decade alone, we have funded nearly 150 research projects to accelerate fundamental research, drug development, and clinical trials in Rett syndrome. Our track record of delivering real results includes funding the discovery that Rett can be reversed, the first gene therapy clinical trial, and the first FDA-⁠⁠approved treatment.