Join IRSF and expert speakers to explore the foundational principles of the genetics of Rett syndrome, including a review of the basic biology processes like transcription and translation that underly genetic-based treatments. We’ll delve into cutting-edge therapeutic genetic approaches, such as RNA therapeutics, gene therapy, and gene editing, and will cover delivery methods and potential side effects. Learn about how outcomes are monitored and optimized.
This live webinar session is free and designed to provide a comprehensive overview of genetic therapeutic advancements for families and caregivers.
Educational resources and support for families provided with thanks to our empowerment sponsor: