Clinical Trial News
Occasionally, Clinical Trial Sponsors will provide community updates or news articles on the status of their study. When available, we will post their updates here.
Trial sponsors are listed below alphabetically.
Clinical Trial Sponsors
DAYBUE™ (trofinetide) approved by FDA for the Treatment of Rett Syndrome 3.10.23
ACADIA Community Update 2.28.23
FDA Grants Priority Review to Trofinetide 9.12.22
ACADIA Submits NDA for Trofinetide 7.18.22 – Community Update | Press Release
ACADIA Trofinetide Top-line Results 12.6.21
(Neuren Pharmaceuticals Top-line Results 12.7.21)
ACADIA Daffodil Update_8.30.21
ACADIA Trofinetide Update 8.4.21
ACADIA Trofinetide Update 3.31.21
ACADIA Trofinetide Update 6.15.20
ACADIA Trofinetide Update 3.23.20
ACADIA Trofinetide Update 2.24.20
ACADIA Trofinetide Update 10.30.19
ACADIA Trofinetide Update 7.31.19
ACADIA Trofinetide Update 5.1.19
ACADIA Trofinetide Update 3.27.19
ACADIA Trofinetide Update 2.3.19
ACADIA Trofinetide Update 12.20.18
For more information, visit ACADIA Pharmaceuticals.
AMO-04 Update 6.13.18
AMO 04QA
For more information, visit AMO-Pharma.
Novartis Update 2.8.21
Novartis Update 9.02.20
Avexis Update 8.20.20
Avexis Update 8.22.19
For more information, visit Novartis Gene Therapies.
Neurogene Announcement 1.23.23 and Letter to Community
Neurogene Announcement 5.18.22 and Letter to Community
For more information, visit Neurogene Inc.
Concluded Trials
Concluded Clinical Trial Sponsors
5.4.20 Newron Reports Top-Line Results from its STARS Study
4.12.19 Newron Thank You
For more information, visit Newron Pharmaceuticals.
Trial Closure Announcement 11.12.20
Trial Criteria_9.6.19
GW Research May, 2019
For more information, visit GW Pharmaceuticals.
