Category

Uncategorized

¡Un logro para Rett: la FDA aprueba Trofinetide para el tratamiento del Síndrome de Rett!

Monday, March 13, 2023

Este tratamiento, el primero de su tipo, está aprobado para personas con síndrome de Rett. Hoy, Acadia Pharmaceuticals anunció que su medicamento en investigación, Trofinetide, ha sido aprobado por la Administración de Alimentos y Medicamentos (FDA) de los Estados Unidos para el tratamiento del síndrome de Rett en pacientes adultas y pediátricas. El medicamento, comercializado … Read More

Pioneers Add to RSO’s Value in Clinical Trial Process

Monday, April 23, 2018

Paige Nues, Director of Family Empowerment Rettsyndrome.org In a world of complexity, I aim for simplicity. My work at Rettsyndrome.org has always been to focus around the age-old basics: Why, What, Where and When. My ‘Why’ started simply: our daughter Katie was diagnosed with Rett syndrome and I couldn’t sit by and wait for someone … Read More

A FIRST FOR RETT: FDA approves Trofinetide for the treatment of Rett syndrome!
It’s Giving Tuesday - Go ALL IN for Rett!

A FIRST FOR RETT: FDA approves Trofinetide for the treatment of Rett syndrome!