November 21, 2024

Raising a Hand: A Journey of Healing, Hope, and Friendship

Inconceivable. That’s the word that photographer Dave Clements uses to describe the emotion swelling in his stomach when thinking back to March 9, 2003. It was that spring afternoon in […]

Acadia Pharmaceuticals Submits Marketing Authorization Application to the European Medicines Agency for Trofinetide for the Treatment of Rett Syndrome

IRSF Leadership Update

After a 7-year tenure, Melissa Kennedy stepped down as CEO at the end of 2024. Board…

Update on Patient SAE & Discontinuation of High Dose Protocol (Community Letter)

Raising a Hand: A Journey of Healing, Hope, and Friendship

Inconceivable. That’s the word that photographer Dave Clements uses to describe the emotion swelling in his…

Update on Patient SAE (Community Letter)

Neurogene Provides Update on NGN-401 Gene Therapy Clinical Trial for Rett Syndrome